Baliforsen sodium structure
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Common Name | Baliforsen sodium | ||
|---|---|---|---|---|
| CAS Number | 1687746-79-7 | Molecular Weight | N/A | |
| Density | N/A | Boiling Point | N/A | |
| Molecular Formula | N/A | Melting Point | N/A | |
| MSDS | N/A | Flash Point | N/A | |
Use of Baliforsen sodiumBaliforsen (sodium) is an antisense oligonucleotide (16 nucleotides) designed to target myotonic dystrophy protein kinase (DMPK) mRNA and treat myotonic dystrophy. |
| Name | Baliforsen sodium |
|---|
| Description | Baliforsen (sodium) is an antisense oligonucleotide (16 nucleotides) designed to target myotonic dystrophy protein kinase (DMPK) mRNA and treat myotonic dystrophy. |
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| Related Catalog | |
| References |
| InChIKey | BQIRWUYCQDIAQA-DEBWEYBYSA-N |
|---|---|
| SMILES | COCCOC1C(O[P+](O)([S-])OCC23OC(n4cc(C)c(N)nc4=O)C(OC2C)C3O[P+](O)([S-])OCC23OC(n4cc(C)c(N)nc4=O)C(OC2C)C3O[P+](O)([S-])OCC2OC(n3cnc4c(=O)[nH]c(N)nc43)CC2O[P+](O)([S-])OCC2OC(n3cnc4c(N)ncnc43)CC2O[P+](O)([S-])OCC2OC(n3cnc4c(N)ncnc43)CC2O[P+](O)([S-])OCC2OC(n3cc(C)c(=O)[nH]c3=O)CC2O[P+](O)([S-])OCC2OC(n3cnc4c(=O)[nH]c(N)nc43)CC2O[P+](O)([S-])OCC2OC(n3cc(C)c(=O)[nH]c3=O)CC2O[P+](O)([S-])OCC2OC(n3cc(C)c(N)nc3=O)CC2O[P+](O)([S-])OCC2OC(n3cc(C)c(N)nc3=O)CC2O[P+](O)([S-])OCC23OC(n4cnc5c(=O)[nH]c(N)nc54)C(OC2C)C3O[P+](O)([S-])OCC23OC(n4cnc5c(N)ncnc54)C(OC2C)C3O[P+](O)([S-])OCC2OC(n3cc(C)c(N)nc3=O)C(OCCOC)C2O[P+](O)([S-])OCC2OC(n3cnc4c(N)ncnc43)C(OCCOC)C2O)C(CO[P+](O)([S-])OC2C(CO)OC(n3cc(C)c(=O)[nH]c3=O)C2OCCOC)OC1n1cc(C)c(N)nc1=O.[Na+].[Na+].[Na+].[Na+].[Na+].[Na+].[Na+].[Na+].[Na+].[Na+].[Na+].[Na+].[Na+].[Na+].[Na+] |