2055732-84-6
2055732-84-6 structure
- Name: Viltolarsen
- Chemical Name: Viltolarsen
- CAS Number: 2055732-84-6
- Molecular Formula:
- Molecular Weight:
- Catalog: Research Areas Others
- Create Date: 2022-01-25 17:32:52
- Modify Date: 2025-08-25 04:13:22
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Viltolarsen (NS-065/NCNP-01), a phosphorodiamidate morpholino antisense oligonucleotide, targets the splicing of exon 53 in the dystrophin gene. Viltolarsen can be used for the research of the Duchenne muscular dystrophy (DMD)[1].
| Name | Viltolarsen |
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| Description | Viltolarsen (NS-065/NCNP-01), a phosphorodiamidate morpholino antisense oligonucleotide, targets the splicing of exon 53 in the dystrophin gene. Viltolarsen can be used for the research of the Duchenne muscular dystrophy (DMD)[1]. |
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| Related Catalog | |
| In Vitro | Duchenne muscular dystrophy (DMD) is one of the most common lethal muscle-wasting disorders affecting young boys caused by mutations in the DMD gene. Exon skipping has emerged as a promising therapy for DMD. Antisense oligonucleotides (AONs) are designed to induce the skipping of exon(s), in order to restore the reading frame, and therefore, allow for dystrophin expression[1]. |
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