| 常用名 | Branaplam hydrochloride | CAS号 | 1562338-39-9 |
|---|---|---|---|
| 价格 | 纯度 | 99.0% | |
| 备货期 | 10天 | 库存 | 现货 |
| 产品详情(用途,包装等)
用途: Branaplam (LMI070; NVS-SM1) hydrochloride is a highly potent, selective and orally active survival motor neuron-2 (SMN2) splicing modulator with an EC50 of 20 nM for SMN. Branaplam hydrochloride inhibits human-ether-a-go-go-related gene (hERG) with an IC50 of 6.3 μM. Branaplam hydrochloride elevates full-length SMN protein and extends survival in a severe spinal muscular atrophy (SMA) mouse model[1][2]. 物理化学性质: CAS号:1562338-39-9 常用中文名:Branaplam hydrochloride 常用英文名:Branaplam hydrochloride 分子式:C22H28ClN5O2 分子量:429.94 密度:N/A 沸点:N/A 熔点:N/A 闪点:N/A |