Safety and efficacy of gene transfer for Leber's congenital amaurosis

AM Maguire, F Simonelli, EA Pierce…

Index: Brimble, Margaret A.; Chan, Seng H. Australian Journal of Chemistry, 1998 , vol. 51, # 3 p. 235 - 242

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Citation Number: 1447

Abstract

... Journal of Clinical Investigation 126, 1198-1207. ... Hironori Uehara, Susie Choi, Lara S. Carroll, Subrata K. Das, Judd M. Cahoon, Brian H. Kirk, Blaine ... Wilson, Shalesh Kaushal, Laura R. Erker, Lauren Jensen, Maureen T. McBride, Terence R. Flotte, Margaret Humphries, Roberto ...